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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Amikacin Liposome Inhalation Suspension for Treatment of Mycobacterium Xenopi Pulmonary InfectionActinomycetales infectious disease, Bacterial Infections and Mycoses, Infections, bacterial infectious disease, gram-positive bacterial infections, lung disorder, mycobacterial infectious disease, respiratory system disorderRecruitingPhase 22025-11-19NCT06585020
National Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and ChildrenBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Niemann-Pick disease, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, histiocytosis, inborn errors of metabolism, lymphatic system disorder, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, non-Langerhans cell histiocytosis, sphingolipidosisNot yet recruitingNot stated2025-05-22NCT06985212