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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Luspatercept in Patients Affected With Rare Inherited AnemiasHereditary Red Blood Cell Disorder (Disorder)Not yet recruitingPhase 22026-01-12NCT07331818
RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Hemolysis, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, alpha thalassemia spectrum, anemia, beta thalassemia, bone marrow disorder, congenital dyserythropoietic anemia, cystinosis, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary anemia, hereditary disease, inborn errors of metabolism, inherited aplastic anemia, inherited hemoglobinopathy, iron metabolism disease, lysosomal storage disease, metabolic disease, myelodysplastic syndrome, pyruvate kinase deficiency of red cells, sickle cell disease, sideroblastic anemia, thalassemiaRecruitingNot stated2024-01-19NCT06213402
Safety and Efficacy of Mitapivat Sulfate in Adult Patients With Erythrocyte MembranopathiesHereditary Red Blood Cell Disorder (Disorder)Not yet recruitingPhase 22023-12-26NCT05935202