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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A 2-Part Study to Assess Efficacy, Safety and Tolerability of BMB-101 for the Treatment of Patients With Prader-Willi Syndrome.Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Prader-Willi syndrome, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutritionNot yet recruitingPhase 22025-12-05NCT07266324
BMB-101 in Absence Epilepsy and DEECongenital, Hereditary, and Neonatal Diseases and Abnormalities, Epilepsies, Myoclonic, Epilepsy, Absence, Epilepsy, Generalized, Epileptic Syndromes, Lennox-Gastaut syndrome, brain disorder, central nervous system disorder, epilepsy, epilepsy with eyelid myoclonia, hereditary disease, nervous system disorderRecruitingPhase 22025-08-12NCT06401538