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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
PDE6A Gene Therapy for Retinitis PigmentosaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, eye disorder, hereditary disease, inherited retinal dystrophy, retinal degeneration, retinal disorder, retinitis pigmentosaActive, not recruitingPhase 1 / Phase 22024-04-18NCT04611503
Safety and Efficacy of rAAV.hCNGA3 Gene Therapy in Patients With CNGA3-linked AchromatopsiaEye Diseases, Hereditary, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, achromatopsia, color vision disorder, cone dystrophy, eye disorder, nervous system disorder, vision disorderActive, not recruitingPhase 1 / Phase 22024-04-18NCT02610582