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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluating the Safety and Preliminary Efficacy of EXG202 Gene Therapy for Neovascular AMDWet Age-related Macular DegenerationNot yet recruitingPhase 1 / Phase 22025-09-17NCT07178249
A Long-term Follow up Study of EXG102-031 in Participants With wAMDWet Age-related Macular DegenerationRecruitingNot stated2025-08-15NCT06859515
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyEnrolling by invitationEarly phase 12025-03-21NCT06888661
To Evaluate the Safety and Preliminary Efficacy of Intravitreal EXG202 Injection in Patients with Wet (neovascular) Age-related Macular Degeneration (wAMD)Wet Age-related Macular Degeneration; Wet Age-related Macular Degeneration (wAMD)Not yet recruitingEarly phase 12025-03-21NCT06888492
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMAcentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyEnrolling by invitationNot stated2025-03-05NCT06588803
The Safety and Efficacy of Intravenous EXG110 in Patients With Fabry DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderNot yet recruitingPhase 1 / Phase 22025-02-11NCT06819514