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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Supporting Weak Immune System During Autoimmune Therapy: Testing Panzyga to Prevent InfectionsBlood Protein Disorders, Hemic and Lymphatic Diseases, Hypogammaglobulinemia, Infections, agammaglobulinemia, hematologic disorder, immune system disorder, inborn error of immunity, lymphatic system disorder, lymphoproliferative syndromeRecruitingPhase 32026-09-29NCT07220915
Study of IV Human Plasma-derived C1 Esterase Inhibitor Concentrate in Patients With Congenital C1-INH Deficiency for Treatment and Pre-procedure Preventing of Acute Hereditary Angioedema AttacksEdema, Hypersensitivity, Immediate, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, immune system disorder, skin disorder, skin vascular disease, urticaria, vascular disorderRecruitingPhase 32026-09-29NCT06361537
Phase 3 Study on the Efficacy and Safety of Human Plasma Derived Antithrombin (Atenativ) in Heparin-Resistant Patients Scheduled to Undergo Cardiac Surgery Necessitating Cardiopulmonary BypassBlood Protein Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, hematologic disorder, hereditary antithrombin deficiency, hereditary disease, inherited blood coagulation disorder, thrombophiliaRecruitingPhase 32026-09-28NCT06096116
Efficacy of Atenativ in Patients With Congenital Antithrombin Deficiency Undergoing Surgery or DeliveryCongenital Antithrombin DeficiencyRecruitingPhase 32026-09-28NCT04918173
Treatment of Hemophilia A Patients With FVIII InhibitorsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingNot stated2026-09-23NCT04023019
Post Marketing Observational Study on Safety of BALFAXAR vs. KCENTRA for Reversal of Vitamin K Antagonist Induced Anticoagulation in Adults Undergoing Urgent Surgery or Invasive Procedurevitamin K-dependent clotting factors, combined deficiency of, type 1Active, not recruitingNot stated2026-09-15NCT06429787
Study to Evaluate the Pharmacokinetics, Efficacy, Tolerability, and Safety of Subcutaneous Human Immunoglobulin (Newnorm) in Patients With Primary Immunodeficiency DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunityActive, not recruitingPhase 32026-08-06NCT04640142
Study to Evaluate Safety and Efficacy of Different PANZYGA Dose Regimens in Pediatric Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) PatientsPediatric Chronic Inflammatory Demyelinating PolyneuropathyRecruitingPhase 32026-08-05NCT04929236
Effectiveness and Tolerability of Eqwilate in Real-life ConditionsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired)Active, not recruitingNot stated2026-07-16NCT04106908
Efficacy, Safety & Utilisation of Nuwiq, Octanate and Wilate in Previously Untreated & Minimally Treated Haemophilia A PatientsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingNot stated2026-06-02NCT03695978
Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for SurgeryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 42026-05-12NCT05936580
Nuwiq for Perioperative Management Of Patients With Haemophilia A on Emicizumab Regular Prophylaxis StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, severe hemophilia ARecruitingPhase 42026-05-12NCT05935358
Observational Study of Subcutaneous Immunoglobulin (Cutaquig) in Patients With Primary and Secondary Immunodeficiency.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunityActive, not recruitingNot stated2026-05-08NCT04354129
Von Willebrand Factor in Pregnancy (VIP) StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Hemorrhage, Obstetric Labor Complications, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postpartum Hemorrhage, Urogenital Diseases, Uterine Hemorrhage, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, pregnancy disorder, puerperal disorder, von Willebrand disease (hereditary or acquired)RecruitingNot stated2025-12-18NCT04146376