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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of RM-718 in Healthy Subjects and Patients With MC4R Pathway ImpairmentAbnormalities, Multiple, Body Weight, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Imprinting Disorders, Male Urogenital Diseases, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Parkes Weber syndrome, Pathological Conditions, Signs and Symptoms, Prader-Willi syndrome, Signs and Symptoms, Urogenital Abnormalities, Urogenital Diseases, chromosomal disorder, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, hereditary disease, hypogonadism, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutritionActive, not recruitingPhase 1 / Phase 22026-10-09NCT06239116
A Trial of Setmelanotide in Acquired Hypothalamic ObesityCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Urogenital Abnormalities, Urogenital Diseases, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, hypogonadismActive, not recruitingPhase 32026-08-10NCT05774756
Real-World Effects of MC4R Agonist Therapy in BBS and Severe Genetic ObesityAbnormalities, Multiple, Alstrom syndrome, Bardet-Biedl syndrome, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Hyperphagia, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Digestive, brain disorder, central nervous system disorder, central nervous system malformation, eye disorder, hereditary disease, hereditary motor and sensory neuropathy, hypothalamic disorder, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, retinitis pigmentosaRecruitingPhase 42026-06-29NCT07674290
A Study of Setmelanotide in Patients With Prader-Willi SyndromeAbnormalities, Multiple, Body Weight, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hyperphagia, Imprinting Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Prader-Willi syndrome, Signs and Symptoms, Signs and Symptoms, Digestive, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutritionActive, not recruitingPhase 22026-02-12NCT06772597
A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)Congenital Abnormalities, Congenital Cranial Dysinnervation Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Ocular Motility Disorders, Optic Nerve Hypoplasia, Urogenital Abnormalities, Urogenital Diseases, central nervous system malformation, corpus callosum, agenesis of, cranial nerve neuropathy, disorder of sexual differentiation, endocrine system disorder, eye disorder, gonadal disorder, gonadal dysgenesis, hereditary disease, hypogonadism, nervous system disorder, optic nerve disorder, pituitary stalk interruption syndrome, septooptic dysplasia, third cranial nerve disorderRecruitingPhase 32026-02-12NCT06760546
A Long-Term Study of Bivamelagon in Participants With Hypothalamic Obesity (HO)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Urogenital Abnormalities, Urogenital Diseases, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, hypogonadismEnrolling by invitationPhase 22026-02-10NCT07156578
Early Genetic Identification of ObesityAbnormalities, Multiple, Bardet-Biedl syndrome, Body Weight, Bone Diseases, Developmental, Ciliopathies, Cognition Disorders, Cognitive Dysfunction, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Hyperphagia, Limb Deformities, Congenital, Musculoskeletal Abnormalities, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Pediatric Obesity, Signs and Symptoms, Signs and Symptoms, Digestive, bone disorder, brain disorder, central nervous system disorder, cognitive disorder, dysostosis, eye disorder, hereditary disease, hypothalamic disorder, musculoskeletal system disorder, nervous system disorder, nutritional disorder, obesity disorder, obesity due to pro-opiomelanocortin deficiency, overnutrition, polydactyly, psychiatric disorder, retinal disorder, retinitis pigmentosa, syndactyly, synostosisActive, not recruitingNot stated2025-09-29NCT06239064