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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of Acoramidis in Patients With Transthyretin Amyloid CardiomyopathyTransthyretin Amyloid Cardiomyopathy (ATTR-CM)RecruitingNot stated2026-09-15NCT07791160
Registre HEAR, Healthcare European Amyloidosis RegistryAmyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, proteostasis deficienciesRecruitingNot stated2021-11-01NCT05101304