Design Therapeutics, Inc.
Design Therapeutics, Inc.
Explore linked clinical trials.3 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| DT-168 in Keratoplasty Patients With Fuchs Endothelial Corneal Dystrophy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Fuchs' endothelial dystrophy, corneal disorder, corneal dystrophy, eye disorder, hereditary disease | Recruiting | Phase 2 | 2026-09-28 | NCT07024693 | |
| A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorder | Recruiting | Phase 1 / Phase 2 | 2025-05-18 | NCT06874010 | |
| A Single Ascending Dose Study of DT-216P2 in Normal Healthy Participants | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorder | Not yet recruiting | Phase 1 | 2025-02-21 | NCT06772870 |