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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase I/II Clinical Study to Evaluate the Safety and Efficacy of VGN-R08b in Patients With Type III Gaucher's DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher Disease, Type 3, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisNot yet recruitingPhase 1 / Phase 22026-05-22NCT07603050
A Safety Study of Contralateral Eye Dosing of VGR-R01 in Participants With Bietti's Crystalline Dystrophy (BCD)Bietti crystalline corneoretinal dystrophyNot yet recruitingPhase 1 / Phase 22026-05-14NCT07586306
A Study to Evaluate the Tolerability, Safety and Efficacy of VGM-R02bglutaryl-CoA dehydrogenase deficiencyRecruitingPhase 12026-05-13NCT06217861
A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R08b in Parkinson's Disease Patients With GBA1 MutationsParkinson disease, basal ganglia disorder, brain disorder, central nervous system disorder, movement disorder, nervous system disorder, neurodegenerative disease, parkinsonian disorder, synucleinopathyNot yet recruitingPhase 1 / Phase 22026-05-01NCT07414290
A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC Deficiencyaromatic L-amino acid decarboxylase deficiencyActive, not recruitingPhase 2 / Phase 32026-04-21NCT06432140
A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Patients With Parkinson's DiseaseParkinson disease, basal ganglia disorder, brain disorder, central nervous system disorder, movement disorder, nervous system disorder, neurodegenerative disease, parkinsonian disorder, synucleinopathyActive, not recruitingPhase 1 / Phase 22026-03-31NCT06480461
VGN-Ex05e in Patients With Autism Spectrum Disorder Associated With Severe Self-Injurious and Aggressive Behaviorsautism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderNot yet recruitingEarly phase 12026-02-25NCT07433517
Study to Evaluate the Efficacy and Safety of VGR-R01 Gene Therapy in Patients With Bietti Crystalline DystrophyBietti crystalline corneoretinal dystrophyActive, not recruitingPhase 32025-12-24NCT06699108
Safety and Tolerability of VGR-R01 for Patients With Bietti Crystalline DystrophyBietti crystalline corneoretinal dystrophyActive, not recruitingPhase 12025-12-24NCT05694598
The Safety and Efficacy of VGO-Cs01p in Patients With CD7-positive Relapsed/Refractory Acute T-lymphoblastic LeukemiaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Precursor T-Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmNot yet recruitingEarly phase 12025-05-15NCT06849401
An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisRecruitingEarly phase 12024-02-22NCT06272149
An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.aromatic L-amino acid decarboxylase deficiencyRecruitingEarly phase 12023-03-13NCT05765981