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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluate the Efficacy and Safety of KK8398 in Patients With Achondroplasia(AOBA Study)Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaActive, not recruitingPhase 32026-10-08NCT06926491
Study of ME-401 in Subjects With Relapsed or Refractory Indolent B-cell Non-Hodgkin's Lymphoma (NHL)Indolent B-cell Non-Hodgkin's LymphomaActive, not recruitingPhase 22026-10-05NCT04533581
MSA-01 in Multiple System Atrophyautonomic nervous system disorder, basal ganglia disorder, brain disorder, central nervous system disorder, movement disorder, multiple system atrophy, nervous system disorder, neurodegenerative disease, primary dysautonomia, synucleinopathyRecruitingPhase 32026-03-04NCT07446894
A Multicenter Multinational Observational Study of Children With HypochondroplasiahypochondroplasiaRecruitingNot stated2025-04-03NCT06212947