University of Florida Health Center for Pediatric Neuromuscular and Rare Diseases
University of Florida Health Center for Pediatric Neuromuscular and Rare Diseases
Gainesville, Florida, United States1 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Open-Label Extension Study of BBP-418 (Ribitol) for LGMD2I/R9 | autosomal recessive limb-girdle muscular dystrophy type 2I | Active, not recruiting | Phase 3 | 2026-07-02 | NCT07678775 |