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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of TYRA-300 in Children With Achondroplasia: BEACH301Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaRecruitingPhase 22026-10-01NCT06842355
Efficacy and Safety of Vamifeport in Adult Participants With Homeostatic Iron Regulator Gene (HFE)-Related Hereditary HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingPhase 22026-09-16NCT07332091
Cerebellar Involvement in Cognitive SequencingEffects of Cerebellar Stimulation on Brain ActivationRecruitingNot applicable2026-09-14NCT06108336
Oral N-acetylglucosamine in Crohn's DiseaseCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderNot yet recruitingPhase 22026-09-11NCT07225998
Use of N-Acetylcysteine in the Treatment of Repetitive and Self-Injurious Behaviors in Cornelia de Lange SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, De Lange Syndrome, Neurobehavioral Manifestations, Neurologic Manifestations, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, psychiatric disorderNot yet recruitingPhase 22026-08-14NCT04381897
Community Health Worker Based Intervention to Improve Palliative Carecancer, neoplasmEnrolling by invitationNot applicable2026-07-23NCT05407844
C-Raven, a Virtual Tobacco Cessation Intervention in Residency ClinicsChemically-Induced Disorders, Tobacco Dependence, nicotine dependence, psychiatric disorder, substance-related disorderActive, not recruitingPhase 42026-07-06NCT07220356
Efficacy of KL1333 in Adult Patients With Primary Mitochondrial DiseaseMuscle Weakness, Neurologic Manifestations, Neuromuscular Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 22026-06-26NCT05650229
Alcohol Treatment Outcomes Following Early vs. Standard Liver Transplant for SAHAlcohol Use Disorder, Chemically-Induced Disorders, Digestive System Diseases, alcohol-induced disorders, alcohol-related disorders, alcoholic hepatitis, alcoholic liver disease, hepatitis, liver disorder, psychiatric disorder, substance-related disorderRecruitingNot applicable2026-06-09NCT03845205
Cerebellar Involvement in Alcohol Use Disorder (AUD)Alcohol Use Disorder, Chemically-Induced Disorders, alcohol-related disorders, psychiatric disorder, substance-related disorderRecruitingNot applicable2026-05-11NCT05732207
Isturisa Treatment in Mild Autonomous Cortisol Secretion( MACS)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Paraneoplastic Endocrine Syndromes, Urogenital Abnormalities, Urogenital Diseases, adrenal gland disorder, adrenogenital syndrome, cardiovascular disorder, congenital adrenal hyperplasia, disorder of sexual differentiation, ectopic ACTH secretion syndrome, endocrine system disorder, gonadal disorder, hereditary disease, hypertensive disorder, inborn errors of metabolism, metabolic disease, neoplasm, paraneoplastic syndrome, steroid inherited metabolic disorder, vascular disorderRecruitingPhase 42026-03-05NCT07247058
Primary Tumor Research and Outcomes NetworkneoplasmRecruitingNot stated2026-02-25NCT02790983
Prospective Observational Study of the ICD in Sudden Cardiac Death PreventionArrhythmias, Cardiac, Death, Death, Sudden, Death, Sudden, Cardiac, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cardiac arrest, cardiomyopathy, cardiovascular disorder, congestive heart failure, heart disorder, heart failureRecruitingNot stated2026-01-20NCT00733590