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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pediatric Evaluation and Registry for Liver Cholestasis in CanadaAbnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1RecruitingNot stated2026-10-08NCT07411716
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 32026-09-28NCT07160634
Pilot Study of IT Topotecan and Maintenance Chemotherapy for HR-EBTs in Children < 6 Years, Post ConsolidationDigestive System Diseases, Medulloblastoma, Childhood, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, Neuroectodermal Tumors, Primitive, Peripheral, atypical teratoid rhabdoid tumor, brain disorder, central nervous system cancer, central nervous system disorder, digestive system disorder, embryonal tumor with multilayered rosettes, ependymoblastoma, epithelial neoplasm, glioma, hypertrophic pyloric stenosis, medulloblastoma, medulloepithelioma, mixed neoplasm, neoplasm, nervous system disorder, neuroblastoma, neuroepithelial neoplasm, pineal body neoplasm, pineoblastoma, primitive neuroectodermal tumor, pyloric stenosis, rhabdoid tumor, stomach disorderRecruitingEarly phase 12026-07-14NCT06942039
Light-Based Monitoring (SR-NIRS) for Suspected Testicular Torsion in ChildrenGenital Diseases, Male Urogenital Diseases, Urogenital Diseases, male reproductive system disorder, spermatic cord torsionNot yet recruitingNot applicable2026-04-23NCT07548086
CLIC-2201 for the Treatment of Relapsed/Refractory B Cell MalignanciesB-cell acute lymphoblastic leukemia, B-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Leukemia, B-Cell, Neoplasms by Histologic Type, Tumor Virus Infections, diffuse large B-cell lymphoma, hematologic disorder, high grade B-cell lymphoma, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, mantle cell lymphoma, neoplasm, non-Hodgkin lymphoma, viral infectious diseaseRecruitingPhase 12026-04-03NCT06208735
Moisturization and Skin Hydration StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypersensitivity, Immediate, Skin Diseases, Eczematous, Skin and Connective Tissue Diseases, atopic eczema, dermatitis, hereditary disease, hereditary skin disorder, immune system disorder, skin disorderNot yet recruitingNot applicable2025-12-08NCT07270965
A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingNot applicable2025-07-08NCT06396325
Internet-delivered Cystic Fibrosis Mental Health Prevention, Wellness, Resource Program: How Does it Work?Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, anxiety disorder, cystic fibrosis, depressive disorder, hereditary disease, lung disorder, pancreas disorder, psychiatric disorder, respiratory system disorderNot yet recruitingNot applicable2025-06-10NCT06020274
Angelman Syndrome Natural History StudyAbnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderRecruitingNot stated2025-04-03NCT04507997
Intranasal Dexmedetomidine Plus Ketamine for Procedural SedationJoint Dislocations, arthropathy, bone fracture, injury, musculoskeletal system disorderRecruitingPhase 2 / Phase 32024-11-05NCT04195256