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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 32026-09-17NCT06612268
A Study Following Males With Haemophilia B on Prophylaxis With Refixia/REBINYNCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderEnrolling by invitationNot stated2026-06-12NCT03745924