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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular DystrophyDuchene Muscular DystrophyRecruitingPhase 2 / Phase 32026-10-02NCT07856329
Open-Label, Long-Term, Extension Study of Infigratinib in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 22026-08-26NCT07393373
Juvenile Inflammatory Rheumatism (JIR) CohorteSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, juvenile idiopathic arthritis, musculoskeletal system disorder, rheumatic disorderEnrolling by invitationNot stated2023-06-15NCT02377245