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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy Trial for CLN6 Batten DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, juvenile neuronal ceroid lipofuscinosis, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseNot yet recruitingPhase 1 / Phase 22026-05-14NCT07582484