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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Cystinosis and Mitochondrial MetabolismCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, cystinosis, hereditary disease, inborn errors of metabolism, lysosomal storage disease, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot applicable2026-08-03NCT07319091