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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Analysis of Velmanase Alfa (Lamzede®)'s Effects in the Body of Children With Alpha-Mannosidosis Under the Age 3Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Mannosidase Deficiency Diseases, Nutritional and Metabolic Diseases, alpha-mannosidosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic diseaseRecruitingNot stated2025-05-16NCT06184503