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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseActive, not recruitingPhase 1 / Phase 22026-09-25NCT04884815