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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Clinical Study to Assess Safety, Efficacy and Pharmacodynamic Profile of GNT0004 in Duchenne Muscular DystrophyDuchene Muscular DystrophyRecruitingPhase 2 / Phase 32026-10-02NCT07856329
Natural History of Duchenne Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-02-12NCT03882827