Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
Shanghai, Shanghai Municipality, China2 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis | Active, not recruiting | Early phase 1 | 2026-08-10 | NCT06528080 | |
| Prospective Clinical Trial for Children With TCRαβ Depleted vs Traditional Haplo Identicle HSCT | graft versus host disease, immune system disorder | Recruiting | Not applicable | 2024-05-29 | NCT06423131 |