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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisActive, not recruitingEarly phase 12026-08-10NCT06528080
Prospective Clinical Trial for Children With TCRαβ Depleted vs Traditional Haplo Identicle HSCTgraft versus host disease, immune system disorderRecruitingNot applicable2024-05-29NCT06423131