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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Clinician Practice Companion to Address Youth Substance UseChemically-Induced Disorders, Drug Misuse, Drug Overdose, Narcotic-Related Disorders, Opioid Use Disorder, Prescription Drug Misuse, Substance Use, cannabis dependence, opiate dependence, psychiatric disorder, substance-related disorderNot yet recruitingNot applicable2026-10-07NCT07725289
Soft-tissue Quadriceps Autograft ACL-reconstruction in the Skeletally-immature vs. HamstringsAnterior Cruciate Ligament Injuries, Knee Injuries, Leg Injuries, injuryRecruitingNot applicable2026-10-07NCT03896464
A Study Evaluating the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of Crovalimab in Pediatric Participants With Atypical Hemolytic Uremic Syndrome (aHUS)Cytopenia, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, atypical hemolytic-uremic syndrome, blood platelet disease, hematologic disorder, hemolytic anemia, hemolytic-uremic syndrome, kidney disorder, thrombocytopenia, thrombotic microangiopathy, uremia, urinary system disorderActive, not recruitingPhase 32026-10-01NCT04958265
BEATRIX: A Study to Learn About a Group B Streptococcus Vaccine in Healthy Pregnant Women and Their BabiesHealthyRecruitingPhase 32026-09-25NCT07160244
Effect of Metformin on Behaviour and the Brain in Children Treated for a Brain TumourCognition Disorders, Cognitive Dysfunction, Medulloblastoma, Childhood, Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, cognitive disorder, epithelial neoplasm, glioma, medulloblastoma, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumor, psychiatric disorderRecruitingPhase 32026-09-24NCT05230758
Diagnosing Asthma With Clinically Accessible, Non-invasive, and Efficient Tests: a Child-inclusive Translational InvestigationHypersensitivity, Immediate, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiratory Hypersensitivity, asthma, bronchial disorder, disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderActive, not recruitingNot stated2026-09-11NCT07011394
Real-World Effectiveness and Safety of Pegcetacoplan in Patients With C3G or IC-MPG: A Multi-Country StudyDisease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Diseases, glomerulonephritis, kidney disorder, nephritis, urinary system disorderRecruitingPhase 42026-09-09NCT07746895
Optimizing Hydroxyurea Dosage With Pharmakokinetic in Patients Suffering of Moderate to Severe Sickle Cell AnemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 2 / Phase 32026-08-21NCT06761560
Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)Abnormalities, Multiple, Arrhythmias, Cardiac, COVID-19, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronaviridae Infections, Down syndrome, Dyssomnias, Edema, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Hemic and Lymphatic Diseases, Hemorrhage, Infant, Newborn, Diseases, Infant, Premature, Diseases, Infections, Inflammation, Kawasaki disease, Lung Injury, Menorrhagia, Menstruation Disturbances, Neurobehavioral Manifestations, Neurologic Manifestations, Nidovirales infectious disease, Nutritional and Metabolic Diseases, Orthocoronavirinae infectious disease, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, Signs and Symptoms, Skin and Connective Tissue Diseases, Sleep Disorders, Intrinsic, Suppuration, Urogenital Diseases, Uterine Hemorrhage, Ventilator-Induced Lung Injury, Water-Electrolyte Imbalance, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, attention deficit hyperactivity disorder, inattentive type, blood coagulation disease, bronchopulmonary dysplasia, cardiovascular disorder, cellulitis, chromosomal disorder, coagulation protein disease, connective tissue disorder, endocrine system disorder, female reproductive system disorder, heart disorder, heart failure, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, hyperaldosteronism, hyperphosphatemia, hypertensive disorder, inherited blood coagulation disorder, insomnia, intellectual disability, lung disorder, lymphatic system disorder, metabolic disease, nervous system disorder, neurodevelopmental disorder, oppositional defiant disorder, pediatric multisystem inflammatory disease, COVID-19 related, phosphorus metabolism disease, pneumonia, potassium deficiency disease, primary aldosteronism, psychiatric disorder, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, respiratory tract infectious disorder, skin disorder, skin disorder caused by infection, skin infection, skin vascular disease, sleep-wake disorder, uterine disorder, vascular disorder, vascular hemostatic disease, vasculitis, viral infectious disease, viral pneumoniaRecruitingNot stated2026-08-21NCT04278404
A Study to Assess the Efficacy and Safety of Ruxolitinib Cream in Children and Adolescents (6 to <18 Years Old) With Moderate Atopic DermatitisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypersensitivity, Immediate, Skin Diseases, Eczematous, Skin and Connective Tissue Diseases, atopic eczema, dermatitis, hereditary disease, hereditary skin disorder, immune system disorder, skin disorderActive, not recruitingPhase 32026-08-19NCT06832618
A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Alectinib in Pediatric Participants With ALK Fusion-Positive Solid or CNS TumorsNeoplasms by Site, central nervous system cancer, neoplasm, nervous system disorderActive, not recruitingPhase 1 / Phase 22026-08-14NCT04774718
Phase 1/2 Study of Mirdametinib + Vinblastine for Newly Diagnosed/Previously Untreated PLGG + Activation of MAPKPediatric Low-grade GliomaRecruitingPhase 1 / Phase 22026-08-11NCT06666348
A Phase II Study of Sunitinib or Temsirolimus in Patients With Advanced Rare TumoursAdvanced Rare TumoursActive, not recruitingPhase 22026-08-11NCT01396408
Comparison of Non-Invasive Mean Arterial Blood Pressure Measurements at the Arm and Ankle During Elective Cesarean Delivery.Blood Pressure Measurement in Pregnancy; Cesarean Delivery; Pregnancy; Skin to Skin ContactRecruitingNot stated2026-08-07NCT07422766
Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative ColitisDigestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisActive, not recruitingPhase 32026-08-03NCT04624230
A Study of Axatilimab at 3 Different Doses in Participants With Chronic Graft Versus Host Disease (cGVHD)Bronchiolitis Obliterans, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderRecruitingPhase 22026-06-16NCT04710576
Study of Individuals Affected With HypoplasminogenemiahypoplasminogenemiaRecruitingNot stated2026-06-04NCT03797495
TINI 2: Total Therapy for Infants With Acute Lymphoblastic Leukemia IIHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 1 / Phase 22026-06-03NCT05848687
A Study to Evaluate the Safety and Efficacy of Axatilimab in Combination With Ruxolitinib in Participants With Newly Diagnosed Chronic Graft-Versus-Host DiseaseBronchiolitis Obliterans, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, graft versus host disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderActive, not recruitingPhase 22026-05-22NCT06388564
A Single Patient Study of Sapropterin for Multisystem Smooth Muscle Dysfunction Syndromemultisystemic smooth muscle dysfunction syndromeNot yet recruitingNot applicable2026-05-07NCT07574034
PROPULSION SANTE: Inflammometry to Improve the Diagnostic Trajectory in Situations of Suspected Asthma in Children and AdultsHypersensitivity, Immediate, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiratory Hypersensitivity, asthma, bronchial disorder, disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderRecruitingNot stated2026-04-30NCT06981169
Trametinib for Pediatric Neuro-oncology Patients With Refractory Tumor and Activation of the MAPK/ERK Pathway.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, brain disorder, central nervous system cancer, central nervous system disorder, epithelial neoplasm, glioma, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, low grade glioma, neoplasm, nerve sheath neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neuroepithelial neoplasm, neurofibroma, neurofibromatosis, neurofibromatosis type 1, neuromuscular disease, peripheral nervous system disorder, peripheral nervous system neoplasm, plexiform neurofibroma, primitive neuroectodermal tumorActive, not recruitingPhase 22026-04-24NCT03363217
PRospective Evaluation of Peripartum Anticoagulation ManaGement for ThrOmboembolismEmbolism and Thrombosis, Thromboembolism, cardiovascular disorder, vascular disorder, venous thromboembolismRecruitingNot stated2025-11-28NCT05756244
Virtual Reality for Pain Management During Dupilumab InjectionCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypersensitivity, Immediate, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Diseases, Eczematous, Skin and Connective Tissue Diseases, anxiety, anxiety disorder, atopic eczema, dermatitis, hereditary disease, hereditary skin disorder, immune system disorder, psychiatric disorder, skin disorderRecruitingNot applicable2025-08-24NCT06182436
Low-value Care, and Variation in Practice for Children Hospitalized With BronchiolitisInfections, bronchial disorder, bronchiolitis, bronchitis, lung disorder, obstructive lung disease, respiratory system disorder, respiratory tract infectious disorderRecruitingNot stated2025-07-23NCT06506474