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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pediatric Evaluation and Registry for Liver Cholestasis in CanadaAbnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1RecruitingNot stated2026-10-08NCT07411716
NIV-NAVA in Infants With Severe Bronchiolitis, a Pilot Multicenter Randomized Controlled TrialInfections, bronchial disorder, bronchiolitis, bronchitis, lung disorder, obstructive lung disease, respiratory system disorder, respiratory tract infectious disorderNot yet recruitingNot applicable2026-09-22NCT07834723
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 22026-09-15NCT05996003
Pilot Study of IT Topotecan and Maintenance Chemotherapy for HR-EBTs in Children < 6 Years, Post ConsolidationDigestive System Diseases, Medulloblastoma, Childhood, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, Neuroectodermal Tumors, Primitive, Peripheral, atypical teratoid rhabdoid tumor, brain disorder, central nervous system cancer, central nervous system disorder, digestive system disorder, embryonal tumor with multilayered rosettes, ependymoblastoma, epithelial neoplasm, glioma, hypertrophic pyloric stenosis, medulloblastoma, medulloepithelioma, mixed neoplasm, neoplasm, nervous system disorder, neuroblastoma, neuroepithelial neoplasm, pineal body neoplasm, pineoblastoma, primitive neuroectodermal tumor, pyloric stenosis, rhabdoid tumor, stomach disorderRecruitingEarly phase 12026-07-14NCT06942039
NS-050/NCNP-03 in Boys With DMD (Meteor50)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 1 / Phase 22026-06-16NCT06053814
BCI@Home: Brain Computer Interface Solutions to Enable Youth Living With Severe DisabilitiesBrain Damage, Chronic, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniocerebral Trauma, brain disorder, brain injury, central nervous system disorder, cerebral palsy, hereditary disease, injury, nervous system disorder, nervous system injuryRecruitingNot applicable2026-05-05NCT07073378
Arm More + Camp: An Implementation StudyBrain Damage, Chronic, Craniocerebral Trauma, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, brain injury, central nervous system disorder, cerebral palsy, cerebral palsy spastic hemiplegic, hemiplegia, injury, nervous system disorder, nervous system injury, palsyEnrolling by invitationNot applicable2026-05-01NCT07065916
Diabetes Transition Coordinator StudyNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusEnrolling by invitationNot applicable2026-05-01NCT06300047
A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingNot applicable2025-07-08NCT06396325
CMV-specific Donor-derived T Lymphocytes for the Treatment of Recalcitrant CMV Infection in a Patient With Primary ImmunodeficiencyT-cell immunodeficiency, cytomegalovirus pneumoniaActive, not recruitingNot applicable2025-06-11NCT07015801
Angelman Syndrome Natural History StudyAbnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderRecruitingNot stated2025-04-03NCT04507997
IMPACT: IMplementation of Physical Activity for Children and Adolescents on Treatmentchildhood malignant neoplasm, neoplasmRecruitingNot applicable2025-03-07NCT04956133