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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatmentscentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingNot stated2023-03-14NCT05768048
Natural History of SMAcentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingNot stated2023-03-06NCT05755451