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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Tight Control of Treatment Adherence and Efficacy by Telemedicine for an Improved Personalized Management of Patients With HemophiliaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingNot applicable2026-10-09NCT07867834
Efficacy and Safety of Zelpultide Alfa in Preterm Neonates at High Risk of Developing Bronchopulmonary Dysplasia (BPD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Infant, Premature, Diseases, Lung Injury, Ventilator-Induced Lung Injury, bronchopulmonary dysplasia, lung disorder, respiratory system disorderRecruitingPhase 2 / Phase 32026-10-09NCT06897839
A Phase 1 Study of LY5830966 in Participants With Primary Myelofibrosis (PMF), Post-Polycythemia Vera Myelofibrosis (PPV-MF), or Post-Essential Thrombocythemia Myelofibrosis (PET-MF) Who Have Been Failed by a Type I JAK2 Inhibitor (JAK2i)Hemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosisRecruitingPhase 12026-10-09NCT06343805
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05444257
Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508delCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05331183
Pulmonary Complications Following TEVARAcute Aortic Syndrome, Aneurysm, Aortic Dissection, Dissection, Blood Vessel, aortic disorder, cardiovascular disorder, vascular disorderActive, not recruitingNot stated2026-10-07NCT07863453
A Non-interventional Study of Participants With BPDCN Treated With ChemotherapyCD4+/CD56+ hematodermic neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Skin and Connective Tissue Diseases, hematologic disorder, hematopoietic and lymphoid system neoplasm, leukemia, lymphoma, malignant histiocytosis, neoplasm, skin disorder, skin neoplasmRecruitingNot stated2026-09-15NCT07785180
A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, anemia, bone marrow disorder, hematologic disorder, hemolytic anemia, myelodysplastic syndrome, paroxysmal nocturnal hemoglobinuriaActive, not recruitingNot stated2026-09-03NCT05776472
Physical Activity and Healthy Aging: Promoting Cardio-metabolic Capacity to Fight Chronic Inflammation and Improve Outcomes in Breast Cancer Patients (PhActHealth Study)Neoplasms by Site, Skin and Connective Tissue Diseases, breast cancer, breast disorder, breast neoplasm, neoplasm, skin disorder, triple-negative breast carcinomaRecruitingNot applicable2026-08-20NCT07776951
Phase 3 Study of Pelabresib (CPI-0610) in Myelofibrosis (MF) (MANIFEST-2)Hemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosisActive, not recruitingPhase 32026-07-17NCT04603495
Digital Twin and Ml-basEd MOdel of TEVAR Interventionsaortic disorder, cardiovascular disorder, vascular disorderRecruitingNot stated2026-06-11NCT07640828
Pirfenidone to Prevent Fibrosis in Ards.Fibrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiration Disorders, adult acute respiratory distress syndrome, interstitial lung disease, lung disorder, pulmonary fibrosis, respiratory system disorderRecruitingPhase 32026-05-08NCT05075161
A Longitudinal Observational Study of the Natural History and Management of Patients With HCCDigestive System Diseases, Digestive System Neoplasms, Liver Neoplasms, Neoplasms by Site, liver disorder, neoplasmActive, not recruitingNot stated2026-04-17NCT02954094
A Prospective Multicenter Study of the Effects of Plant-based Diets on Gut Microbiome and Derived Metabolites in Patients Affected by Smoldering Multiple MyelomaBlood Protein Disorders, Hemic and Lymphatic Diseases, Hypergammaglobulinemia, hematologic disorder, immune system disorder, immunoproliferative disorder, monoclonal gammopathy, neoplasm, precancerous condition, smoldering plasma cell myelomaRecruitingNot applicable2026-04-03NCT07069751
Assess Abdominal Aortic Diameter in FemalesAneurysm, aortic aneurysm, aortic disorder, cardiovascular disorder, vascular disorderRecruitingNot stated2026-03-27NCT07487961
The Italian Transthyretin Amyloidosis Web-NetworkImmunoglobulin Light-chain Amyloidosis, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, amyloidosis, immune system disorder, immunoproliferative disorder, lymphoproliferative syndrome, metabolic disease, monoclonal gammopathy, neoplasm, plasma cell neoplasm, proteostasis deficienciesRecruitingNot stated2026-03-27NCT05444920
Efficacy and Safety of XyloCore Peritoneal Dialysis Solution.Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderRecruitingPhase 32026-03-24NCT03994471
CACP: Study on Camptodactyly - Arthropathy - Coxa Vara - Pericarditis (CACP) SyndromeBone Anteversion, Bone Malalignment, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Torsion Abnormality, arthropathy, bone disorder, cardiovascular disorder, coxa vara, disease, heart disorder, musculoskeletal system disorder, pericarditis, syndromic diseaseRecruitingNot stated2026-03-16NCT07468461
National Multicentre Study on Lipid Profile in Noonan Syndrome and Related Disorders: Trends by Age, Gender and GenotypeCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, cardiovascular disorder, congenital heart disease, connective tissue disorder, heart disorder, musculoskeletal system disorderRecruitingNot stated2026-03-11NCT07464821
A Study of Elritercept Alone or Together With Ruxolitinib in Adults With MyelofibrosisCytopenia, Hemic and Lymphatic Diseases, Myeloproliferative Disorders, anemia, blood platelet disease, bone marrow disorder, hematologic disorder, primary myelofibrosis, thrombocytopeniaRecruitingPhase 22026-02-05NCT05037760
RecruitmEnt Assessed by eleCtRical Impedance TomographyRespiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderRecruitingNot stated2025-05-20NCT04460859
A Multicenter Multinational Observational Study of Children With HypochondroplasiahypochondroplasiaRecruitingNot stated2025-04-03NCT06212947
Outcomes of Empiric Antibiotic Therapy Based on Hospital Antibiograms in Organ Transplant Recipients with BacteraemiaBacterial Infections and Mycoses, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Systemic Inflammatory Response Syndrome, bacterial infectious disease, bacterial infectious disease with sepsisEnrolling by invitationNot stated2025-03-13NCT06874920
Pentaglobin in CRE and PA Neutropenic InfectionsBacterial Infections and Mycoses, Cytopenia, Febrile Neutropenia, Hemic and Lymphatic Diseases, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Pseudomonas infection, Sepsis, Shock, Systemic Inflammatory Response Syndrome, agranulocytosis, bacterial infectious disease, gram-negative bacterial infections, hematologic disorder, leukocyte disorder, leukopenia, neutropenia, toxic shock syndromeActive, not recruitingPhase 22025-01-06NCT03494959
MaaT013 As Salvage Therapy in Ruxolitinib Refractory GI-aGVHD PatientsAcute Graft Versus Host Disease in Intestine; Steroid Refractory GVHDActive, not recruitingPhase 32024-10-17NCT04769895