Rare Disease Research
Rare Disease Research
Iselin, New Jersey, United States1 results ยท Page 1 of 1
Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| First-in-human Study of UX016 in GNEM | GNE myopathy | Recruiting | Phase 1 / Phase 2 | 2026-09-03 | NCT07511556 |