45 results · Page 1 of 2

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05444257
Pridopidine Phase 3 Study to Evaluate Efficacy and Safety in ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingPhase 32026-10-06NCT07322003
Efficacy and Safety of Vamifeport in Adult Participants With Homeostatic Iron Regulator Gene (HFE)-Related Hereditary HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingPhase 22026-09-16NCT07332091
A Non-interventional Study of Participants With BPDCN Treated With ChemotherapyCD4+/CD56+ hematodermic neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Skin and Connective Tissue Diseases, hematologic disorder, hematopoietic and lymphoid system neoplasm, leukemia, lymphoma, malignant histiocytosis, neoplasm, skin disorder, skin neoplasmRecruitingNot stated2026-09-15NCT07785180
ENVISION IDE Trial: Safety and Effectiveness of NAVITOR in Transcatheter Aortic Valve ImplantationVentricular Outflow Obstruction, aortic valve disorder, aortic valve stenosis, cardiovascular disorder, heart disorder, heart valve disorderEnrolling by invitationNot applicable2026-09-11NCT05932615
Tenofovir Exposures in Advanced Kidney Disease StudyChronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderNot yet recruitingNot stated2026-09-10NCT07812571
Polycystic Kidney Disease 1 (PKD1) Gene Variant Groups in Autosomal Dominant Polycystic Kidney DiseaseAbnormalities, Multiple, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, autosomal dominant polycystic kidney disease, cystic kidney disease, hereditary disease, kidney disorder, polycystic kidney disease, urinary system disorderActive, not recruitingNot stated2026-09-09NCT06747572
A Study to Evaluate IPN10200 Safety and Efficacy in the Prevention of Episodic or Chronic Migraine in AdultsChronic Migraine; Episodic MigraineActive, not recruitingPhase 22026-09-08NCT06625060
A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)Hemic and Lymphatic Diseases, Hemoglobinuria, Paroxysmal, anemia, bone marrow disorder, hematologic disorder, hemolytic anemia, myelodysplastic syndrome, paroxysmal nocturnal hemoglobinuriaActive, not recruitingNot stated2026-09-03NCT05776472
Revumenib in Combination With Azacitidine + Venetoclax in Patients NPM1-mutated or KMT2A-rearranged AMLHemic and Lymphatic Diseases, Neoplasms by Histologic Type, acute myeloid leukemia, hematologic disorder, leukemia, myeloid leukemia, neoplasmRecruitingPhase 32026-09-02NCT06652438
Intensive Weight Loss Intervention Versus Bariatric Surgery for Adults With Severe and Complex Obesity: the LightBAR Randomised TrialBody Weight, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, nutritional disorder, obesity disorder, overnutritionRecruitingNot applicable2026-08-21NCT06309238
CGM Use in Adults With Type 2 Diabetes on Basal InsulinNutritional and Metabolic Diseases, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, type 2 diabetes mellitusActive, not recruitingNot applicable2026-08-21NCT05944432
A Phase 2 Study Evaluating Safety and Tolerability of RCT2100 (CFTR mRNA) in Healthy Participants and in Participants With CFCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 22026-08-19NCT06237335
OSTEOMICS: Identifying Regulators of Bone HomeostasisBone Diseases, Metabolic, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, arthritic joint disease, arthropathy, bone disorder, bone fracture, bone marrow disorder, hematologic disorder, injury, metabolic disease, musculoskeletal system disorder, osteoarthritis, osteoporosis, rheumatic disorderRecruitingNot stated2026-08-14NCT05732870
A Treatment Study Protocol for Participants 0-45 Years With Acute Lymphoblastic LeukaemiaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 32026-08-12NCT04307576
A Trial of CHOP-R Therapy, With or Without Acalabrutinib, in Patients With Newly Diagnosed Richter's SyndromeB-cell neoplasm, Hemic and Lymphatic Diseases, Leukemia, B-Cell, Neoplasms by Histologic Type, Richter transformation, diffuse large B-cell lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasmActive, not recruitingPhase 22026-08-07NCT03899337
Less Invasive Surfactant Administration in Late Preterm or Early Term Born InfantsPulmonary Atelectasis, Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderRecruitingNot applicable2026-08-06NCT06421506
Fibrosis Lessens After Metabolic SurgeryBody Weight, Digestive System Diseases, Fibrosis, Fibrosis, Liver, Nutritional and Metabolic Diseases, Overweight, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, cirrhosis of liver, fatty liver disease, liver disorder, metabolic dysfunction-associated steatotic liver disease, nutritional disorder, obesity disorder, overnutritionRecruitingPhase 42026-07-31NCT06374875
KYSA-6: A Study of Anti-CD19 Chimeric Antigen Receptor T-Cell Therapy, in Patients With Generalized Myasthenia GravisNeoplasms by Site, Paraneoplastic Syndromes, Nervous System, autoimmune disease, autoimmune disorder of the nervous system, immune system disorder, myasthenia gravis, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, paraneoplastic syndromeRecruitingPhase 2 / Phase 32026-07-29NCT06193889
"Physiological vs Right Ventricular Pacing Outcome Trial Evaluated for bradyCardia Treatment" (PROTECT-HF)Arrhythmias, Cardiac, Bradycardia, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cardiovascular disorder, heart disorderRecruitingNot applicable2026-07-22NCT05815745
Optimizing the Use of Aspirin for the Prevention of PreeclampsiaFemale Urogenital Diseases and Pregnancy Complications, Urogenital Diseases, hypertension, pregnancy-induced, preeclampsia, pregnancy disorderNot yet recruitingPhase 32026-06-24NCT07665853
Physiological Versus Right Ventricular Outcome Trial Evaluated for Bradycardia Treatment Upgradescardiovascular disorder, heart disorder, heart failureRecruitingNot applicable2026-06-23NCT06052475
EMBRACE- BLOOM - Building Literacy and Outcomes Through Observation and Monitoring: Information Needs and Wearable Data in Pregnancy CouplesPregnancyNot yet recruitingNot stated2026-06-03NCT07623096
A Study of the Safety and Activity of Sparsentan for the Treatment of Patients With Immunoglobulin A NephropathyFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, IgA glomerulonephritis, Male Urogenital Diseases, Urogenital Diseases, autoimmune disease, glomerulonephritis, immune system disorder, kidney disorder, nephritis, urinary system disorderRecruitingPhase 22026-06-03NCT04663204
Heart Failure Carer Support Programme: Implementation Testing in the UK.cardiovascular disorder, heart disorder, heart failureRecruitingNot applicable2026-06-02NCT07373041