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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Open-Label Extension of EDG-5506 in Participants With Becker Muscular DystrophyBecker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseEnrolling by invitationPhase 22026-09-17NCT06066580
Non-interventional Study of Seroprevalence of Pre-existing Antibodies Against Adenovirus-associated Virus Vector (AAV9) and the Progression of Disease in Patients With Plakophilin 2 (PKP2)-Associated Arrhythmogenic Right Ventricular Cardiomyopathy (ARVC)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, arrhythmogenic right ventricular cardiomyopathy, cardiomyopathy, cardiovascular disorder, congenital heart disease, heart disorder, heart failureRecruitingNot stated2024-11-01NCT06311708
A Study to Evaluate XEN1101 as Adjunctive Therapy in Focal Epilepsybrain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorderActive, not recruitingPhase 22024-09-24NCT03796962