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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Trial of Setmelanotide in Acquired Hypothalamic ObesityCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Urogenital Abnormalities, Urogenital Diseases, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, hypogonadismActive, not recruitingPhase 32026-08-10NCT05774756
An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCIDCongenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Infant, Newborn, Diseases, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunity, metabolic disease, severe combined immunodeficiency, severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiencyEnrolling by invitationNot stated2025-12-18NCT04049084
A Study to Evaluate Tovorafenib in Pediatric and Young Adult Participants With Relapsed or Progressive Low-Grade Glioma and Advance Solid Tumorslow grade gliomaRecruitingPhase 22025-04-10NCT04775485