Hopital Necker-Enfants Malades
Hopital Necker-Enfants Malades
Paris, France2 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| To Assess the Efficacy, Safety, and Tolerability of INCB000928 in Participants With Fibrodysplasia Ossificans Progressiva | Ossification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificans | Recruiting | Phase 2 | 2026-05-22 | NCT05090891 | |
| A Natural History Study in Children With a Type II Collagen Disorder With Short Stature | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Kniest dysplasia, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, Strudwick syndrome, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondrogenesis, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, spondyloepiphyseal dysplasia congenita | Recruiting | Not stated | 2023-10-02 | NCT05408715 |