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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
To Assess the Efficacy, Safety, and Tolerability of INCB000928 in Participants With Fibrodysplasia Ossificans ProgressivaOssification, Heterotopic, Pathologic Processes, Pathological Conditions, Signs and Symptoms, muscle tissue disorder, musculoskeletal system disorder, myositis disease, myositis ossificansRecruitingPhase 22026-05-22NCT05090891
A Natural History Study in Children With a Type II Collagen Disorder With Short StatureBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Kniest dysplasia, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, Strudwick syndrome, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondrogenesis, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, spondyloepiphyseal dysplasia congenitaRecruitingNot stated2023-10-02NCT05408715