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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Personalized Antisense Oligonucleotide Therapy for Participants With TARDBP ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderEnrolling by invitationPhase 1 / Phase 22026-08-03NCT07743268
Personalized Antisense Oligonucleotide for Participants With CHCHD10 ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderEnrolling by invitationPhase 1 / Phase 22026-07-13NCT07095686
Personalized Antisense Oligonucleotide for a Single Participant With CHCHD10 ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderActive, not recruitingPhase 1 / Phase 22026-07-13NCT06977451