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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-term Psychological and Cognitive Evaluation of Children Treated With Allogeneic Hematopoietic Stem Cell Transplantation for ImmunodeficiencyALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; Primary ImmunodeficienciesRecruitingNot stated2026-09-25NCT07766304
Mentalization and Social Cognition in Adolescents After Suicide AttemptParasomnias, nervous system disorder, psychiatric disorder, sleep-wake disorderNot yet recruitingNot applicable2026-09-18NCT07688798
Longitudinal Assessment of Protein Markers in the Cerebrospinal Fluid of Patients With Central Nervous System Involvementcentral nervous system disorder, nervous system disorderNot yet recruitingNot stated2026-09-09NCT07313098
A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 22026-09-09NCT06128564
A Comparative Study of Fusional Vergence According to Ocular Dominance in Healthy SubjectsNo Eye DisorderRecruitingNot stated2026-08-26NCT07697131
INNODIA Family & Friends Early-Stage T1D Detection ProtocolNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose intolerance, glucose metabolism disease, hyperglycemia, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingNot stated2026-08-24NCT07118098
Prospective Clinical Assessment Study in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaRecruitingNot stated2026-07-16NCT06410976
Evaluation of Therapeutic Adherence Among Patients Followed in the Department of Hereditary Metabolic Diseases at Necker HospitalNutritional and Metabolic Diseases, metabolic diseaseRecruitingNot stated2026-06-30NCT07356557
Assessment of Airway Opening Pressure in Invasively Ventilated ChildrenRespiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderRecruitingNot applicable2026-06-30NCT07262541
Assessment of Body Composition in Children Treated With Growth Hormone for the Indication of Isolated Non-acquired Growth Hormone Deficiency.Isolated Non-acquired Growth Hormone DeficiencyRecruitingNot stated2026-06-24NCT07333521
Role of Bile Acids and Microbiota in Clostridioides Difficile Infection in Ulcerative ColitisBacterial Infections and Mycoses, Clostridium infectious disease, Digestive System Diseases, Infections, bacterial infectious disease, colitis, colonic disorder, digestive system disorder, gastroenteritis, gram-positive bacterial infections, inflammatory bowel disease, intestinal disorder, ulcerative colitisRecruitingNot stated2026-06-24NCT06228352
Evaluation of Software for Interpreting Virological Results Indicated for the Diagnosis of Cytomegalovirus (CMV) Infection During Pregnancy and Intended for Health ProfessionalsDNA Virus Infections, Herpesviridae infectious disease, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cytomegalovirus infection, disease, viral infectious diseaseRecruitingNot stated2026-06-08NCT06694428
Primitive Immunodeficiency, Intrauterine Devices and Menstrual Hygiene ProductsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunityRecruitingNot stated2026-06-08NCT06519734
Congenital Aniridia Patient QuestionnaireCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Abnormalities, Eye Diseases, Hereditary, aniridia, eye disorder, hereditary disease, iris disorder, uveal disorderRecruitingNot stated2026-06-02NCT05390801
Denys-Drash Syndrome and Risk of Post-transplant Lymphoproliferative Disorder46 XY differences of sex development, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Denys-Drash syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Urogenital Abnormalities, Urogenital Diseases, Urogenital Neoplasms, Wilms tumor, benign urinary system neoplasm, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hereditary disease, hereditary neoplastic syndrome, kidney cancer, kidney disorder, mixed neoplasm, neoplasm, urinary system disorderNot yet recruitingNot stated2026-05-26NCT07605884
Epidemiological Data on Mast Cell Pathologies in FranceMast Cell Activation Disorders, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, immune system disorder, mastocytosis, neoplasmRecruitingNot stated2026-04-22NCT06186856
Characterization of Social Cognition Profiles in Children and Adolescents With Neurodevelopmental Disorders: a Clinical Study Using a Multidimensional Batteryattention deficit hyperactivity disorder, inattentive type, autism spectrum disorder, neurodevelopmental disorder, oppositional defiant disorder, pervasive developmental disorder, psychiatric disorderRecruitingNot applicable2026-04-16NCT07439276
Respiratory Muscles and Work of Breathing in ChildrenCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hernia, Hernia, Diaphragmatic, Internal Hernia, Neurologic Manifestations, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Respiration Disorders, Signs and Symptoms, Spinal Curvatures, bone disorder, cardiovascular disorder, congenital diaphragmatic hernia, heart disorder, lung disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, palsy, respiratory failure, respiratory paralysis, respiratory system disorder, scoliosis, vertebral column disorderRecruitingNot applicable2026-04-03NCT05051254
Sleep-disordered Breathing and Neurocognitive Assessment in Children and Young AdultsApnea, Dyssomnias, Respiration Disorders, Sleep Disorders, Intrinsic, nervous system disorder, respiratory system disorder, sleep apnea syndrome, sleep-wake disorderRecruitingNot applicable2026-04-03NCT04971850
Virtual Reality in Children With and Without Vestibular DeficitsEar Diseases, inner ear disorder, otorhinolaryngologic disease, vestibular disorderRecruitingNot applicable2026-04-03NCT04791748
Use of Eye Tracking to Study Social Perception Abnormalities in Children With Angelman SyndromeAbnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderRecruitingNot stated2026-03-16NCT06737718
Experiences Reported by Siblings of Children Hospitalized in the PICUStress Disorders, Traumatic, acute stress disorder, post-traumatic stress disorder, psychiatric disorderRecruitingNot stated2025-12-01NCT06664333
Physiology and Pathologies Linked to Human Splenic Function : Direct and Ex-vivo Perfusion ExplorationsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Infections, Mosquito-Borne Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, hereditary spherocytosis, inherited hemoglobinopathy, malaria, parasitic infectious disease, protozoa infectious disease, sickle cell disease, vector-borne diseaseRecruitingNot stated2025-09-15NCT06418256
Measurement of Brain Perfusion by a MR Perfusion Imaging Called eASL in Children's Cerebral Arteriopathies.Cerebral ArteriopathyRecruitingNot stated2025-09-15NCT05026060
Quantification of Motor Function in Infants With Spinal Muscular Atrophy Treated With Innovative Therapiescentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyActive, not recruitingNot applicable2025-09-15NCT04833348