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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Evaluate XEN1101 as Adjunctive Therapy in Primary Generalized Tonic-Clonic Seizuresbrain disorder, central nervous system disorder, epilepsy, nervous system disorderRecruitingPhase 32026-10-08NCT05667142
PREEMIE: Study for Treatment of PDA in Premature InfantsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, patent ductus arteriosusActive, not recruitingNot applicable2026-10-07NCT06587282
A Study to Evaluate the Pharmacokinetics, Safety and Efficacy of Afimkibart (RO7790121) in Children With Moderately to Severely Active Ulcerative ColitisModerately to Severely Active Ulcerative ColitisRecruitingPhase 32026-10-06NCT07158242
Pyruvate Kinase Deficiency Global Longitudinal RegistryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, congenital nonspherocytic hemolytic anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, pyruvate kinase deficiency of red cellsActive, not recruitingNot stated2026-09-28NCT03481738
Alpha-Defensin and Synovial Proteins to Improve Detection of Pediatric Septic ArthritisInfections, arthritic joint disease, arthropathy, bacterial arthritis, musculoskeletal system disorderRecruitingNot applicable2026-07-29NCT03704766
ARDS in Children and ECMO Initiation Strategies Impact on Neurodevelopment (ASCEND)Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderActive, not recruitingNot stated2026-07-14NCT05388708
Advanced SPinal Innovations With Robotics and Enabling Technology Registryadolescent idiopathic scoliosis, bone disorder, idiopathic scoliosis, musculoskeletal system disorder, spondylolisthesis, spondylolysis, spondylosis, vertebral column disorderRecruitingNot stated2026-06-22NCT05071144
HeadStart4: Newly Diagnosed Children (<10 y/o) With Medulloblastoma and Other CNS Embryonal TumorsNeoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, epithelial neoplasm, glioma, medulloblastoma, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumorActive, not recruitingPhase 42026-06-03NCT02875314
ONC201 in H3 K27M-mutant Diffuse Glioma Following Radiotherapy (the ACTION Study)Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, epithelial neoplasm, glioma, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumorRecruitingPhase 32026-04-16NCT05580562
SELVA: A Phase 3 Study Evaluating QTORIN 3.9% Rapamycin Anhydrous Gel in the Treatment of Microcystic Lymphatic MalformationsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Lymphatic Abnormalities, Neoplasm, Lymphatic Tissue, Neoplasms by Histologic Type, cardiovascular disorder, lymphangioma, lymphatic system disorder, microcystic lymphatic malformation, neoplasm, vascular malformationActive, not recruitingPhase 32026-03-27NCT06239480
Casting vs Bracing for Idiopathic Early-Onset ScoliosisEarly-Onset Scoliosis Deformity of Spine; Scoliosis IdiopathicActive, not recruitingNot applicable2026-03-13NCT04500041
Congenital Heart Disease GEnetic NEtwork Study (CHD GENES)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderActive, not recruitingNot stated2026-01-30NCT01196182
Pediatric ACL: Understanding Treatment OptionsAnterior Cruciate Ligament ReconstructionActive, not recruitingNot stated2025-05-13NCT02772770
Evaluation of the MuSICCA for Measuring AwarenessConsciousness Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, cognitive disorder, nervous system disorder, psychiatric disorderRecruitingNot stated2025-04-30NCT04050995
The Tether™ - Vertebral Body Tethering System Post Approval StudyScoliosis IdiopathicRecruitingNot stated2024-02-22NCT04505579