Cincinnati Children's
Cincinnati Children's
Cincinnati, Ohio, United States5 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Assess the Incidence of Skin Cancers in Patients With Epidermolysis Bullosa Receiving Filsuvez | Collagen Diseases, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin Abnormalities, Skin and Connective Tissue Diseases, connective tissue disorder, epidermolysis bullosa, epidermolysis bullosa dystrophica, hereditary disease, hereditary skin disorder, junctional epidermolysis bullosa, skin disorder, vesiculobullous skin disease | Recruiting | Not stated | 2026-09-28 | NCT06423573 | |
| AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Active, not recruiting | Phase 2 / Phase 3 | 2026-07-21 | NCT05693142 | |
| ARPKD Database Study | Abnormalities, Multiple, Agenesis of Cerebellar Vermis, Bardet-Biedl syndrome, Caroli disease, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Meckel syndrome, type 1, Polycystic Kidney, Autosomal Recessive, Urogenital Diseases, bile duct cyst, bile duct disorder, biliary tract disorder, brain disorder, central nervous system disorder, cystic kidney disease, eye disorder, hereditary disease, hypothalamic disorder, isolated congenital hepatic fibrosis, kidney disorder, nephronophthisis, nephronophthisis 1, nervous system disorder, polycystic kidney disease, retinitis pigmentosa, urinary system disorder | Recruiting | Not stated | 2026-06-15 | NCT01401998 | |
| Pediatric Radio Frequency Coils Generic | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, Musculoskeletal Abnormalities, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Active, not recruiting | Not stated | 2026-06-12 | NCT01633866 | |
| SARC038: Phase 2 Study of Regorafenib and Nivolumab in Osteosarcoma | Neoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, neoplasm, osteosarcoma, sarcoma | Active, not recruiting | Phase 2 | 2025-10-31 | NCT04803877 |