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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of CD19 Targeted CAR T Cell Therapy in Pediatric Patients With Relapsed or Refractory B Cell Acute Lymphoblastic Leukemia (B ALL) and Aggressive Mature B-cell Non-Hodgkin Lymphoma (B NHL)B-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Disease Attributes, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Recurrence, Tumor Virus Infections, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, viral infectious diseaseRecruitingPhase 12026-10-09NCT06173518
Evaluation of Maralixibat in Pruritus Associated With General Cholestatic Liver Disease (EXPAND)Cholangitis, Sclerosing, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, bile duct disorder, biliary atresia, biliary tract disorder, cholangitis, skin disorderActive, not recruitingPhase 32026-10-06NCT06553768
Prenatally-initiated Psychological Intervention for Mothers of Infants With Congenital Heart Disease (CHD)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot applicable2026-09-10NCT07582861
BOND: Direct Breastfeeding to Enhance Maternal and Infant Health in Congenital Heart DiseaseCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot applicable2026-09-10NCT07582848
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilatorscongenital structural myopathy, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 1 / Phase 22026-09-03NCT07052929
PheCheck™ Validation StudyBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingNot stated2026-08-25NCT07551921
Illuminate: A Clinical Study Evaluating CAR T Immune Cell Therapy (BCB-276) for Patients With Diffuse Intrinsic Pontine Glioma (DIPG).Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, brain disorder, brain stem glioma, brainstem cancer, central nervous system cancer, central nervous system disorder, central nervous system neoplasm, childhood malignant neoplasm, diffuse intrinsic pontine glioma, epithelial neoplasm, glioma, neoplasm, nervous system disorder, neuroepithelial neoplasm, primitive neuroectodermal tumorRecruitingPhase 22026-08-04NCT07680439
Trial of Indication-Based Transfusion of Red Blood Cells in ECMOPathologic Processes, Pathological Conditions, Signs and Symptoms, Shock, multiple organ dysfunction syndromeActive, not recruitingNot applicable2026-07-02NCT05405426
Cast or Operation for Medial Epicondyle Fracture Treatment in ChildrenArm Injuries, Elbow Fractures, Elbow Injuries, bone fracture, injuryRecruitingNot applicable2026-07-01NCT05131672
The Pediatric ALL Evaluation and TrialAnterior Cruciate Ligament Injuries, Anterior Cruciate Ligament Tear, Knee Injuries, Leg Injuries, injuryRecruitingNot applicable2026-05-29NCT04825587
Esophageal String Test in Eosinophilic EsophagitisDigestive System Diseases, Eosinophilia, Hemic and Lymphatic Diseases, Hypersensitivity, Immediate, digestive system disorder, eosinophilic esophagitis, esophageal disorder, esophagitis, gastroenteritis, hematologic disorder, immune system disorder, leukocyte disorderActive, not recruitingNot stated2026-05-15NCT02008903
Indocyanine Green (ICG) Guided Sentinel Lymph Node Mapping for Pediatric Visceral Solid TumorsSolid TumorRecruitingEarly phase 12026-05-04NCT05645523
Surgical or Medical TreatmentBody Weight, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Pediatric Obesity, Signs and Symptoms, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, nutritional disorder, obesity disorder, overnutrition, type 2 diabetes mellitusActive, not recruitingPhase 42026-03-24NCT04128995
Prospective Multisite Study of Quality of Life in Pediatric Intestinal FailureDigestive System Diseases, Hyperphagia, Intestinal Failure, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Signs and Symptoms, Signs and Symptoms, Digestive, digestive system disorder, intestinal disorder, malabsorption syndrome, short bowel syndromeRecruitingNot stated2026-03-23NCT04629014
A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)Congenital Abnormalities, Congenital Cranial Dysinnervation Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Ocular Motility Disorders, Optic Nerve Hypoplasia, Urogenital Abnormalities, Urogenital Diseases, central nervous system malformation, corpus callosum, agenesis of, cranial nerve neuropathy, disorder of sexual differentiation, endocrine system disorder, eye disorder, gonadal disorder, gonadal dysgenesis, hereditary disease, hypogonadism, nervous system disorder, optic nerve disorder, pituitary stalk interruption syndrome, septooptic dysplasia, third cranial nerve disorderRecruitingPhase 32026-02-12NCT06760546
Evaluation of the GORE PV1 Device in Patients With Pulmonary Valve DysfunctionCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ventricular Outflow Obstruction, cardiovascular disorder, congenital heart disease, heart disorder, heart valve disorder, pulmonary valve insufficiency, pulmonary valve stenosis, tetralogy of fallotActive, not recruitingNot applicable2026-02-05NCT03441971
Fontan Udenafil Exercise Longitudinal Assessment Trial - 2Single Ventricle Heart DiseaseRecruitingPhase 32025-10-28NCT05918211
Implementing Models for Mechanical Circulatory Support Presurgical Assessment in Congenital Heart Disease TreatmentCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot applicable2025-10-10NCT03891160
Studying Health Outcomes After Treatment in Patients With RetinoblastomaEye Diseases, Hereditary, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, epithelial neoplasm, eye disorder, intraocular retinoblastoma, neoplasm, neuroepithelial neoplasm, ocular cancer, primitive neuroectodermal tumor, retinal cancer, retinal disorder, retinoblastoma, unilateral retinoblastomaRecruitingNot stated2025-09-19NCT03932786
Clinical Data Registry of Amblyopia Patients on Luminopia TreatmentNeurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, amblyopia, brain disorder, central nervous system disorder, eye disorder, nervous system disorder, vision disorderRecruitingNot stated2025-09-12NCT06429280
International Registry of Congenital Portosystemic Shunt (IRCPSS)46,XX disorder of sex development, Brain Diseases, Metabolic, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hepatic Insufficiency, Hyperammonemia, Hyperandrogenism, Insulin Resistance, Liver Neoplasms, Male Urogenital Diseases, Neoplasms by Site, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenogenital syndrome, brain disorder, cardiovascular disorder, central nervous system disorder, congenital portosystemic shunt, disorder of sexual differentiation, endocrine system disorder, glucose metabolism disease, gonadal disorder, hepatic encephalopathy, hepatopulmonary syndrome, hyperinsulinism, hypertensive disorder, hypoglycemia, liver disorder, liver failure, lung disorder, metabolic disease, neoplasm, nervous system disorder, pulmonary hypertension, respiratory system disorder, vascular disorder, vascular malformationEnrolling by invitationNot stated2025-06-18NCT06041906
KIR Favorable Mismatched Haplo Transplant and KIR Polymorphism in ALL/AML/MDS Allo-HCT ChildrenHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute myeloid leukemia, bone marrow disorder, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, myelodysplastic syndrome, myeloid leukemia, neoplasmEnrolling by invitationPhase 22025-05-04NCT02646839
Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 42022-10-19NCT04687020