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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Natural History to Assess Disease in Patients With MPS IIICCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3CNot yet recruitingNot stated2026-07-17NCT07712003