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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent ThalassemiaNon-Transfusion-dependent Alpha-Thalassemia; Non-Transfusion-dependent Beta-ThalassemiaRecruitingPhase 32026-09-28NCT07517133
A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)Transfusion-dependent Alpha-Thalassemia; Transfusion-dependent Beta-ThalassemiaRecruitingPhase 32026-09-28NCT07506863