Lysosomal & Rare Disorders Research & Treatment Center, Inc

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease	Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder	Active, not recruiting	Phase 1 / Phase 2	2024-04-08		NCT04519749

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