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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Efficacy and Safety of TYRA-300 in Participants With FGFR3 Altered Low Grade, Intermediate Risk Non-Muscle Invasive Bladder CancerFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Non-Muscle Invasive Bladder Neoplasms, Urogenital Diseases, Urogenital Neoplasms, benign urinary system neoplasm, carcinoma, epithelial neoplasm, neoplasm, urinary bladder disorder, urinary bladder neoplasm, urinary system disorderRecruitingPhase 22026-09-29NCT06995677
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 22026-09-15NCT05996003
Efficacy and Safety of 4F-PCC (4-Factor Prothrombin Complex Concentrate) in Adult Patients Undergoing Complex Cardiovascular Surgery With Cardiopulmonary Bypass (CPB)Complex Cardiovascular Surgery With Cardiopulmonary BypassRecruitingPhase 32026-08-18NCT07094087
PROACTIVE-HF IDE Trial Heart Failure NYHA Class IIIcardiovascular disorder, heart disorder, heart failureActive, not recruitingNot applicable2026-07-24NCT04089059
Open-Label Extension Study of BBP-418 (Ribitol) for LGMD2I/R9autosomal recessive limb-girdle muscular dystrophy type 2IActive, not recruitingPhase 32026-07-02NCT07678775
PROACTIVE-HF-2 Trial Heart Failure NYHA Class II and IIIcardiovascular disorder, heart disorder, heart failureRecruitingNot applicable2026-06-29NCT05934487
An Extension Study to Assess Long-Term Safety of Eplontersen in Adults With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)Nutritional and Metabolic Diseases, amyloidosis, metabolic disease, proteostasis deficienciesEnrolling by invitationPhase 32026-04-17NCT05667493
A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS)familial chylomicronemia syndrome, familial lipoprotein lipase deficiencyActive, not recruitingPhase 32025-12-12NCT05130450
Phosphatase Inhibition by Intracoronary Gene Therapy in Subjects With Non-Ischemic NYHA Class III Heart Failurecardiovascular disorder, congestive heart failure, heart disorder, heart failureActive, not recruitingPhase 22025-12-03NCT05598333
CORE-OLE: A Study of Olezarsen (ISIS 678354) Administered Subcutaneously to Participants With Severe Hypertriglyceridemia (SHTG)Dyslipidemias, Lipid Metabolism Disorders, Nutritional and Metabolic Diseases, hyperlipidemia, hypertriglyceridemia, metabolic diseaseActive, not recruitingPhase 32025-12-01NCT05681351