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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
PREEMIE: Study for Treatment of PDA in Premature InfantsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, patent ductus arteriosusActive, not recruitingNot applicable2026-10-07NCT06587282
ALTERRA Post-Approval StudyCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, heart valve disorder, pulmonary valve insufficiency, tetralogy of fallotActive, not recruitingNot stated2026-10-05NCT05378386
A Study to Evaluate the Efficacy and Safety of Cannabidiol Oral Solution (CBD-OS [GWP42003-P, JZP926]) for the Treatment of Focal-Onset SeizuresNeurologic Manifestations, Pathological Conditions, Signs and Symptoms, Seizures, Focal, Signs and Symptoms, nervous system disorder, visual epilepsyRecruitingPhase 12026-10-02NCT07233239
Randomized Study in Children and Adolescents With Migraine: Acute TreatmentEar Diseases, Nausea, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Photophobia, Sensation Disorders, Signs and Symptoms, Signs and Symptoms, Digestive, brain disorder, central nervous system disorder, eye disorder, headache disorder, hearing disorder, hyperacusis, hypnic headache, migraine disorder, nervous system disorder, otorhinolaryngologic disease, vision disorderRecruitingPhase 32026-09-24NCT04649242
Study of the Pharmacokinetics, Safety, and Tolerability of ZONISADE in Children 1 Month to 17 Years of Age With Partial-onset SeizuresNeurologic Manifestations, Pathological Conditions, Signs and Symptoms, Seizures, Focal, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorder, visual epilepsyNot yet recruitingPhase 42026-09-15NCT06534502
A Study of EPX-100 (Clemizole Hydrochloride) in Participants With Dravet SyndromeEpilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, nervous system disorder, visual epilepsyRecruitingPhase 32026-09-15NCT04462770
Prenatally-initiated Psychological Intervention for Mothers of Infants With Congenital Heart Disease (CHD)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot applicable2026-09-10NCT07582861
BOND: Direct Breastfeeding to Enhance Maternal and Infant Health in Congenital Heart DiseaseCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot applicable2026-09-10NCT07582848
Safety and Efficacy Study of Cenobamate in Pediatric Subjects 2-17 Years of Age With Partial-onset (Focal) SeizuresNeurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorder, visual epilepsyActive, not recruitingPhase 32026-09-09NCT05067634
ASCEND: Safety and Tolerability of ION337 for the Treatment of Dravet SyndromeEpilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, brain disorder, central nervous system disorder, epilepsy, nervous system disorderRecruitingPhase 1 / Phase 22026-09-03NCT07531745
Study to Determine if BHV-7000 is Effective and Safe in Adults With Refractory Focal Onset EpilepsyDrug Resistant Epilepsy, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorder, visual epilepsyActive, not recruitingPhase 2 / Phase 32026-08-13NCT06309966
The NODE-202 Study (Study of Etripamil Nasal Spray in Pediatric Patients)Arrhythmias, Cardiac, Cardiac Conduction System Disease, Paroxysmal Supraventricular Tachycardia, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Tachycardia, cardiovascular disorder, heart disorder, ventricular tachycardiaRecruitingPhase 22026-07-21NCT05763953
ARDS in Children and ECMO Initiation Strategies Impact on Neurodevelopment (ASCEND)Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderActive, not recruitingNot stated2026-07-14NCT05388708
Milrinone for Prevention of Post-ligation Cardiac Syndrome TrialPost-ligation Cardiac SyndromeRecruitingPhase 32026-07-01NCT06679855
A Multi-Center Diagnostic Stewardship Program to Improve Respiratory Culture Utilization in Critically Ill ChildrenDisease Attributes, Healthcare-Associated Pneumonia, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Pneumonia, Ventilator-Associated, iatrogenic disease, lung disorder, nosocomial infection, pneumonia, respiratory system disorder, respiratory tract infectious disorder, tracheobronchitisEnrolling by invitationNot stated2026-06-08NCT04987840
Effect of Giving Reduced Fluid in Children After TraumaCritical Illness, Disease Attributes, Multiple Trauma, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, injuryRecruitingNot applicable2026-05-07NCT04201704
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseEnrolling by invitationNot stated2026-05-04NCT06270719
Long-term Safety and Tolerability of BHV-7000Drug Resistant Epilepsy, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, epilepsy, focal epilepsy, nervous system disorder, visual epilepsyEnrolling by invitationPhase 22026-05-01NCT06443463
Improving Safety and Quality of Tracheal Intubation Practice in Pediatric ICUsFailed or Difficult Intubation, Sequela; Intubation Complication; Intubation; DifficultRecruitingNot stated2026-01-09NCT02493478
Multi-Center Molecular Diagnosis and Host Response of Respiratory Viral Infections in Pediatric Transplant RecipientsHematopoietic Cell Transplant; Respiratory Viral Infection; Solid Organ TransplantRecruitingNot stated2025-10-02NCT05550298
National Collaborative to Improve Care of Children With Complex Congenital Heart DiseaseCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, hypoplastic left heart syndromeRecruitingNot stated2025-06-19NCT02852031
Global Utilization And Registry Database for Improved heArt preservatioNCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, heart failureEnrolling by invitationNot stated2025-05-31NCT04141605
Gastric Feeding Versus Transpyloric Feeding in Infants with Severe Bronchopulmonary Dysplasia, a Crossover StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Infant, Premature, Diseases, Lung Injury, Ventilator-Induced Lung Injury, bronchopulmonary dysplasia, lung disorder, respiratory system disorderRecruitingNot applicable2025-02-12NCT06821776