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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Survey of Maribavir Tablets in Participants With Cytomegalovirus InfectionCytomegalovirus (CMV)RecruitingNot stated2026-08-07NCT06577363
A Database Survey to Evaluate the Safety of Immune Globulin Subcutaneous (Human), 20% Solution in Participants With Primary ImmunodeficiencyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, hereditary disease, immune system disorder, inborn error of immunityRecruitingNot stated2026-08-07NCT06565078
A Survey of Susoctocog Alfa (Genetical Recombination) in Participants With Acquired Haemophilia Aacquired hemophilia ARecruitingNot stated2026-08-07NCT06461533
A Survey of Lanadelumab in Participants With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingNot stated2026-08-04NCT05397431
A Study of Freeze-dried Human Protein C Concentrate (TAK-662) in Participants With Congenital Protein C DeficiencyBlood Protein Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, hematologic disorder, hereditary disease, hereditary thrombophilia due to congenital protein C deficiency, inherited blood coagulation disorder, thrombophiliaRecruitingNot stated2026-07-31NCT06590974
A Survey of Brentuximab Vedotin in Pediatric Participants With Hodgkin LymphomaHemic and Lymphatic Diseases, Hodgkins lymphoma, Neoplasms by Histologic Type, immune system disorder, immunoproliferative disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasmRecruitingNot stated2026-04-13NCT05481437
An Observational Study of Vonicog Alfa (rVWF) in Pediatric Participants With Von Willebrand Disease (vWD)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired)RecruitingNot stated2026-02-23NCT07404644
A Database Study of Maralixibat (TAK-625) in Participants With Alagille Syndrome (ALGS) and Progressive Familial Intrahepatic Cholestasis (PFIC)Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1RecruitingNot stated2026-02-20NCT07293897
A Survey of Darvadstrocel in People With Crohn's DiseaseCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderRecruitingNot stated2025-11-17NCT05113095