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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaRecruitingPhase 2 / Phase 32026-09-24NCT07441876
Efficacy and Safety of Vamifeport in Adult Participants With Homeostatic Iron Regulator Gene (HFE)-Related Hereditary HemochromatosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, iron metabolism disease, iron poisoning, metabolic diseaseRecruitingPhase 22026-09-16NCT07332091
Cooling in Mild EncephalopathyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, perinatal asphyxiaRecruitingPhase 32026-02-06NCT05889507
Pharmacokinetics of Antiretroviral Agents in HIV-infected Pregnant Women.Blood-Borne Infections, Genital Diseases, HIV infectious disease, Infections, RNA Virus Infections, Urogenital Diseases, immune system disorder, inborn error of immunity, infectious disease, lentivirus infection, sexually transmitted disease, uterine carcinosarcoma, viral infectious disease, viral sexually transmitted diseaseRecruitingNot stated2025-01-13NCT00825929