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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Non-invasive Functional Assessment and Pathogenesis of Morquio ABone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Mucopolysaccharidosis Type IV A, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorderRecruitingNot stated2026-05-13NCT05284006