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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of TAK-755 in Participants With Congenital Thrombotic Thrombocytopenic PurpuraCytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, blood coagulation disease, blood platelet disease, hematologic disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombophilia, thrombotic microangiopathy, thrombotic thrombocytopenic purpuraActive, not recruitingPhase 32026-04-02NCT04683003
Acute GVHD Suppression Using Costimulation Blockade to Expand Non-malignant TransplantBone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, anemia, aplastic anemia, bone marrow disorder, familial hemolytic anemia, graft versus host disease, hematologic disorder, hemolytic anemia, hereditary disease, immune system disorder, inherited aplastic anemia, inherited hemoglobinopathy, metabolic disease, sickle cell disease, thalassemiaActive, not recruitingPhase 22026-02-25NCT03924401