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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study of SRP-1003 in Participants With Type 1 Myotonic DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseEnrolling by invitationPhase 1 / Phase 22026-10-05NCT06138743
A Study Observing Everyday Effectiveness and Safety of the Drug Elafibranor in Participants With Primary Biliary Cholangitis Who Are Receiving Ongoing TreatmentDigestive System Diseases, Fibrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, bile duct disorder, biliary tract disorder, cholestasis, cirrhosis of liver, intrahepatic cholestasis, liver disorder, primary biliary cholangitisActive, not recruitingNot stated2026-10-01NCT06447168
Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, hematologic disorder, hereditary disease, inherited hemoglobinopathy, metabolic diseaseRecruitingPhase 1 / Phase 22026-09-16NCT00920972
A Study to Determine the Safety and Effectiveness of the Investigational Cellular Therapy GCAR1 in a Patient With Alveolar Soft Part SarcomaNeoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, alveolar soft part sarcoma, myomatous neoplasm, neoplasm, sarcomaActive, not recruitingEarly phase 12026-08-04NCT07104682
Heart Attack Research Program- Imaging StudyInfarction, Necrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cardiovascular disorder, heart disorder, ischemic disease, myocardial infarction, myocardial ischemia, vascular disorderActive, not recruitingNot stated2026-03-19NCT02905357
Left vs Left Randomized Clinical TrialArrhythmias, Cardiac, Cardiac Conduction System Disease, Pathologic Processes, Pathological Conditions, Signs and Symptoms, atrioventricular block, atrioventricular dissociation, cardiovascular disorder, heart disorder, heart failureRecruitingNot applicable2025-10-02NCT05650658
Remote Ischemic Conditioning in PPMSCNS demyelinating autoimmune disease, autoimmune disease, autoimmune disorder of the nervous system, demyelinating disease, immune system disorder, multiple sclerosis, nervous system disorderNot yet recruitingNot applicable2024-05-09NCT06171334