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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Extreme Morphology and Metabolic HealthCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, skeletal dysplasiaActive, not recruitingNot stated2025-02-10NCT05991609