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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Ribociclib in Combination With Everolimus and Dexamethasone in Relapsed ALLHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmActive, not recruitingPhase 12026-08-21NCT03740334
Osteogenesis Imperfecta Trial of AGA2115 for ADUlts With COL1A1 and/or COL1A2 GeNetic Variations (IDUN)Bone Diseases, Developmental, Collagen Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia, osteogenesis imperfectaRecruitingPhase 22026-08-17NCT07062588
A Study to Evaluate a New Semi-rigid Brace, the RESILIENT Brace by Thinks Works, as a Way to Limit Curve Worsening in Kids With Idiopathic Scoliosis.Spinal Curvatures, bone disorder, idiopathic scoliosis, musculoskeletal system disorder, scoliosis, vertebral column disorderRecruitingNot applicable2026-06-01NCT07574632
Casting vs Bracing for Idiopathic Early-Onset ScoliosisEarly-Onset Scoliosis Deformity of Spine; Scoliosis IdiopathicActive, not recruitingNot applicable2026-03-13NCT04500041
Sirolimus in Combination With Metronomic Chemotherapy in Children With Recurrent and/or Refractory Solid and CNS TumorsEwing sarcoma, Hemic and Lymphatic Diseases, Histiocytosis, Langerhans-Cell, Myosarcoma, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, Neuroectodermal Tumors, Primitive, Peripheral, brain disorder, cancer, carcinoma, central nervous system cancer, central nervous system disorder, connective tissue neoplasm, ependymoma, epithelial neoplasm, glioma, histiocytosis, interstitial lung disease, lung disorder, lymphatic system disorder, medulloblastoma, mixed neoplasm, myomatous neoplasm, neoplasm, nervous system disorder, neuroblastoma, neuroepithelial neoplasm, osteosarcoma, pineal body neoplasm, primitive neuroectodermal tumor, respiratory system disorder, rhabdoid tumor, rhabdomyosarcoma, sarcomaActive, not recruitingPhase 22026-03-02NCT02574728
Acute GVHD Suppression Using Costimulation Blockade to Expand Non-malignant TransplantBone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, anemia, aplastic anemia, bone marrow disorder, familial hemolytic anemia, graft versus host disease, hematologic disorder, hemolytic anemia, hereditary disease, immune system disorder, inherited aplastic anemia, inherited hemoglobinopathy, metabolic disease, sickle cell disease, thalassemiaActive, not recruitingPhase 22026-02-25NCT03924401
Simple Bone Cysts in KidsCysts, bone disorder, musculoskeletal system disorder, neoplasm, solitary bone cystRecruitingPhase 32023-07-12NCT02193841