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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3AActive, not recruitingPhase 12026-09-08NCT06567769