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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSHCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3ARecruitingPhase 2 / Phase 32026-09-22NCT02716246